RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...

Columnist Shalom Lim is sad to say goodbye to his caregiver of 18 years, but looks forward to the new chapter of life this ...

A young man with Duchenne MD and treated with Elevidys has died of acute liver failure, Sarepta reports; it's working with ...

Capricor Therapeutics’ investigational therapy deramiocel (CAP-1002) is being considered for approval in the U.S.

Columnist Betty Vertin has a day of heightened awareness about her sons' experience with wheelchairs and life with DMD.

An onslaught of new setbacks due to FSHD disease progression has left columnist Robin Stemple understandably anxious about ...

A comprehensive care approach can help people with ambulatory DMD maximize function and retain the ability to walk for as ...